Case Study Voyager Therapeutics, Inc. - 822 Words

VOYAGER THERAPEUTICS, INC. is a growing Clinical stage Gene Therapy Company. The main focus of this company is based on developing life changing treatments for patients suffering from various types of disease associated with central nervous system or CNS. The gene therapy is called AAV or adeno-associated virus, which is a therapeutic approach to alter the expression of a specific protein, thereby reducing the symptom experienced by patients, and that, will have a clinically meaningful impact on the patient’s life. The company has created a product engine to engineer, optimize manufacture and deliver AAV based gene therapy which would have a sustainable efficacy that follows a single administration directly to the CNS. The product engine has launched a program to address the underlying cause or the predominant manifestation of CNS disease which includes five most common CNS indications; Parkinson’s disease, Friedreich s ataxia, Huntington s disease, spinal muscular atro phy, and Multiple, sclerosis. Mission: As the numbers of people suffering from CNS diseases are on the rise, treatment option still remains limited for many CNS diseases. Therefore, significant unmet medical need for these diseases allows AAV Gene therapy to transform the lives of many patients. The most significant aspect of AAV gene therapy is that, it is targeted therapy which could be an effective alternative medication. Moreover, gene therapy will have a durable and meaningful benefits to the patient.Show MoreRelatedHistory and Moral Development of Mental Health Treatment and Involuntary Commitment10378 Words   |  42 Pagesillness as an organic disturbance, he treated it by psychological methods, minimizing the use of drugs and other physical treatments. Treatments included encouraging reading, entertainment, sea voyagers, etc. Soranus thought that the patient should be engaged in intellectual activities not only for therapeutic purposes but to detect the progress of the illness; accordingly, patients should be en couraged to talk to philosophers to banish their fear and sorrow (Meinsma, R. 1998). Aristotle defined